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Trials & R&D · first seen 2h ago, updated 2h ago

To get drugmakers into ultra-rare disease, the answer isn’t rare disease at all

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OXFORD, England — Making rare disease treatments economically attractive for drugmakers requires looking outside rare disease, according to experts interviewed by Endpoints News. The pharmaceutical industry’s lack of investment in ultra-rar…

Summary from Endpoints News.

Coverage 1 article · 1 outlet

  1. Endpoints News
    To get drugmakers into ultra-rare disease, the answer isn’t rare disease at all